Gene Therapy: Applications of Adeno-associated Viruses and Adenoviruses

This course provides a comprehensive overview of gene therapy, focusing on the fundamentals of genetic diseases and the techniques used to treat them.

Key topics covered include:

• Genetic Diseases: Understanding the causes, types, inheritance patterns, and testing methods for genetic diseases.
• Gene Therapy Delivery: Exploring the use of viral vectors, particularly adeno-associated viruses (AAV) and adenoviruses, to deliver therapeutic genes into cells.
• Viral Vectors: Discussing the replication cycles, advantages, and disadvantages of AAV and adenoviruses in gene therapy.
• Ethical Considerations: Examining the ethical implications of gene therapy, including patient risks, consent, and potential societal impacts.

By completing this course, learners will gain a solid foundation in the principles and applications of gene therapy, enabling them to appreciate its potential benefits and challenges.